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{"id":8614,"date":"2024-12-18T17:10:48","date_gmt":"2024-12-18T21:10:48","guid":{"rendered":"https:\/\/cru.mcgill.ca\/?p=8614"},"modified":"2024-12-19T11:36:18","modified_gmt":"2024-12-19T15:36:18","slug":"retour-sur-2024","status":"publish","type":"post","link":"https:\/\/cru.mcgill.ca\/fr\/retour-sur-2024\/","title":{"rendered":"Retour sur les avanc\u00e9es de 2024"},"content":{"rendered":"\n[et_pb_section fb_built=”1″ fullwidth=”on” _builder_version=”4.9.10″ _module_preset=”default” background_enable_color=”off” width=”100%” max_width=”100%” min_height=”77px” height=”100px” max_height=”100px” custom_margin=”||||false|false” custom_padding=”34px||||false|false” global_module=”4368″ saved_tabs=”all” width__hover_enabled=”on|desktop”][\/et_pb_section][et_pb_section fb_built=”1″ fullwidth=”on” admin_label=”Section” _builder_version=”4.9.10″ module_alignment=”center” custom_margin=”-80px||38px||false|false” custom_padding=”0px|0px|0|0px|false|false” box_shadow_style=”preset1″ box_shadow_vertical=”6px” box_shadow_blur=”37px” box_shadow_spread=”8px” global_module=”3032″ saved_tabs=”all”][et_pb_fullwidth_menu menu_id=”25″ menu_style=”centered” fullwidth_menu=”off” dropdown_menu_bg_color=”#353535″ dropdown_menu_line_color=”rgba(0,0,0,0)” dropdown_menu_text_color=”#ffffff” mobile_menu_bg_color=”rgba(0,0,0,0.67)” _builder_version=”4.9.10″ menu_font=”Fabriga||||||||” menu_text_color=”#ffffff” menu_font_size=”15px” menu_line_height=”0em” background_color=”#1e1e1e” background_size=”initial” background_position=”top_left” background_repeat=”repeat” background_layout=”dark” width=”100%” module_alignment=”left” height=”52px” custom_margin=”-12px||||false|false” custom_margin_last_edited=”off|desktop” custom_padding=”0px||0px||false|false”][\/et_pb_fullwidth_menu][\/et_pb_section][et_pb_section fb_built=”1″ admin_label=”Hero” _builder_version=”4.9.10″ custom_padding=”0|100px|0|100px|false|false” bottom_divider_height=”0px” border_width_bottom=”1px” border_color_bottom=”#efefef”][et_pb_row column_structure=”3_4,1_4″ make_equal=”on” _builder_version=”4.9.10″ width=”100%” max_width=”100%” min_height=”1084px” custom_margin=”|||” custom_margin_tablet=”||0px|” custom_margin_phone=”” custom_margin_last_edited=”on|desktop” custom_padding=”|50px||50px|false|false” use_custom_width=”on” width_unit=”off” custom_width_percent=”100%”][et_pb_column type=”3_4″ _builder_version=”4.3.4″ custom_padding=”||6%|12%|false|false” custom_padding_tablet=”|50px|50px|50px|false|false” custom_padding_phone=”” custom_padding_last_edited=”on|tablet” padding_tablet=”50px|50px|50px|50px” padding_last_edited=”on|tablet” custom_padding__hover=”|||”][et_pb_text _builder_version=”4.9.10″ header_font_size=”45px” custom_margin=”|||1px||” custom_padding=”46px||0px|||”]

2024: Le Neuro \u00e9largit son offre d’essais cliniques testant des th\u00e9rapies cibl\u00e9es pour les maladies g\u00e9n\u00e9tiques<\/strong><\/h1>[\/et_pb_text][et_pb_image src=”https:\/\/cru.mcgill.ca\/wp-content\/uploads\/Year-in-Review-2024-1.jpg” title_text=”Banners Web 2020 – 3″ align=”center” _builder_version=”4.9.10″ _module_preset=”default”][\/et_pb_image][et_pb_text admin_label=”Text” _builder_version=”4.9.10″ text_font_size=”17px” text_line_height=”1.5em” header_font_size=”19px” header_2_font_size=”39px” width=”99.4%” custom_margin=”|66px|||false|false” custom_padding=”5px||0px|0px||”]

\u00a0<\/i><\/h4>\n

Sophie Lorenzo<\/em>
19 d\u00e9cembre 2024<\/span><\/em><\/p>\n

Cette ann\u00e9e, une vague de nouvelles th\u00e9rapies \u00e0 base d’ARN ainsi qu’une toute premi\u00e8re th\u00e9rapie g\u00e9nique ont ouvert un nouveau chapitre \u00e0 l’Unit\u00e9 de recherche clinique du Neuro (URC).<\/p>\n

Ces traitements par ARN et ADN pour des maladies g\u00e9n\u00e9tiques rares sont sur le point d\u2019avoir un impact direct<\/p>\n

sur la progression des maladie \u2013 bien au-del\u00e0 de la gestion de sympt\u00f4mes \u2013 offrant ainsi un vent de changement et d’espoir aux patients.<\/p>\n

\u00a0<\/strong><\/p>\n

Une premi\u00e8re en th\u00e9rapie g\u00e9nique au Canada<\/strong><\/p>\n

Ce fut une ann\u00e9e importante pour l\u2019URC: nous avons men\u00e9 la toute premi\u00e8re \u00e9tude de th\u00e9rapie g\u00e9nique au Neuro, qui s’est \u00e9galement av\u00e9r\u00e9e \u00eatre le premier essai de th\u00e9rapie g\u00e9nique pour la d\u00e9mence au Canada.<\/p>\n

Le traitement de pointe \u00e9tudi\u00e9 dans cet essai de phase 1 est une th\u00e9rapie \u00e0 vecteur viral \u00e0 dose unique pour les personnes atteintes de d\u00e9mence frontotemporale avec la mutation de la progranuline (GRN). Les chercheurs esp\u00e8rent qu\u2019en d\u00e9livrant une copie fonctionnelle du g\u00e8ne GRN, le corps pourra alors augmenter la production de prot\u00e9ine progranuline, ralentissant la progression de cette d\u00e9mence \u00e0 d\u00e9but pr\u00e9coce.<\/p>\n

En savoir plus\u00a0: https:\/\/cru.mcgill.ca\/fr\/genique-ftd.<\/p>\n

Traitements \u00e0 ARN pour une maladie rare surrepr\u00e9sent\u00e9e au Qu\u00e9bec <\/strong><\/p>\n

Apr\u00e8s des ann\u00e9es avec peu d\u2019options de traitement pour la dystrophie myotonique, un essai au Neuro teste une th\u00e9rapie prometteuse qui cible le probl\u00e8me g\u00e9n\u00e9tique au c\u0153ur de cette maladie rare qui touche 1 personne sur 500 Saguenay-Lac-St-Jean.<\/p>\n

Si ce m\u00e9dicament est approuv\u00e9, ce serait le premier \u00e0 pouvoir changer le cours de la maladie, plut\u00f4t que de simplement palier des sympt\u00f4mes.<\/p>\n

En savoir plus\u00a0: https:\/\/cru.mcgill.ca\/fr\/dystrophie-myotonique.<\/p>\n

 <\/p>\n

La recherche qu\u00e9b\u00e9coise explore une nouvelle piste pour stopper la SLA<\/strong><\/p>\n

Trouver un moyen de r\u00e9parer les dommages caus\u00e9s par la SLA au niveau de la jonction neuromusculaire, qui relie les cellules nerveuses et musculaires, constituerait une \u00e9tape majeure dans le traitement de la maladie.<\/p>\n

Les recherches pr\u00e9cliniques de Richard Robitaille, professeur et chercheur \u00e0 l’Universit\u00e9 de Montr\u00e9al, ont d\u00e9montr\u00e9 que la darif\u00e9nacine, un traitement approuv\u00e9 pour l’hyperactivit\u00e9 v\u00e9sicale, pourrait bloquer les cellules hyperactives qui causent la rupture de la connexion nerf-muscle dans la SLA, am\u00e9liorant ainsi la mobilit\u00e9 et la force. Un essai clinique est en cours au Neuro pour valider si cet effet se traduira chez les humains.<\/p>\n

En savoir plus\u00a0: https:\/\/cru.mcgill.ca\/fr\/jonctionneuromusc\/.<\/p>\n

Peut-on enrayer la maladie d\u2019Alzheimer?
<\/strong>Des traitements r\u00e9cemment approuv\u00e9s contre la maladie d\u2019Alzheimer contribuent \u00e0 \u00e9liminer les plaques amylo\u00efdes dans le cerveau, aidant les individus atteints \u00e0 vivre avec une maladie \u00e0 \u00e9volution plus lente. Bien que ce soit une avanc\u00e9e importante, ces m\u00e9dicaments ne peuvent r\u00e9parer les dommages d\u00e9j\u00e0 caus\u00e9s.<\/p>\n

Toutefois, un essai clinique au Neuro cherche \u00e0 \u00e9valuer si un nouveau traitement qui pourrait potentiellement freiner l\u2019accumulation d\u2019amylo\u00efde avant m\u00eame qu\u2019elle ne commence \u2013 une nouvelle \u00e9tape qui pourrait contribuer \u00e0 stopper le d\u00e9veloppement de la maladie.<\/p>\n

En savoir plus\u00a0: https:\/\/cru.mcgill.ca\/fr\/alzheimer-amyloide.<\/p>\n

\u00a0<\/strong><\/p>\n

Atteindre les cellules immunitaires du cerveau pour traiter la scl\u00e9rose en plaques<\/strong><\/p>\n

Parmi les traitements les plus efficaces contre la SP on retrouve les anticorps monoclonaux. Parce qu\u2019ils sont trop gros pour traverser la barri\u00e8re h\u00e9mato-enc\u00e9phalique, leur efficacit\u00e9 se voit limit\u00e9.<\/p>\n

Des chercheurs pensent avoir trouv\u00e9 un moyen d\u2019engager les r\u00e9cepteurs de la barri\u00e8re h\u00e9mato-enc\u00e9phalique et de permettre \u00e0 certaines grosses mol\u00e9cules comme des anticorps utilis\u00e9s dans les traitement novateurs de la traverser. Un nouvel essai au Neuro esp\u00e8re montrer que cette technique permettrait \u00e0 un traitement d’atteindre les cellules immunitaires du cerveau et de calmer l\u2019inflammation sous-jacente qui peut couver entre les rechutes de SP. <\/p>\n

En savoir plus: https:\/\/cru.mcgill.ca\/fr\/barriere-hematocephalique.<\/p>\n

Une seconde chance pour les patients atteints de tumeurs c\u00e9r\u00e9brales<\/strong>
Chaque jour, 27 personnes au Canada sont diagnostiqu\u00e9es avec une tumeur c\u00e9r\u00e9brale, dont le tiers sont malignes. Les qu\u00e9b\u00e9cois et qu\u00e9b\u00e9coises qui sont trait\u00e9s au Neuro b\u00e9n\u00e9ficient d\u2019un acc\u00e8s \u00e0 des m\u00e9decins de renomm\u00e9e mondiale et a des essais cliniques de pointe qui, souvent, ne sont pas offerts ailleurs au Qu\u00e9bec.<\/p>\n

D\u00e9couvrez le parcours d\u2019une patiente qui a re\u00e7u une deuxi\u00e8me chance gr\u00e2ce aux soins prodigu\u00e9s au Neuro suite \u00e0 une r\u00e9cidive de glioblastome, une forme tr\u00e8s agressive de cancer du cerveau<\/p>\n

En savoir plus\u00a0:\u00a0https:\/\/cru.mcgill.ca\/fr\/tumeurs-cerebrales.<\/p>\n

Pour plus d\u2019informations sur les essais en cours au Neuro<\/strong>, visitez cru.mcgill.ca\/fr, ou contactez (514) 398-5500 ou info-CRU.neuro@mcgill.ca.<\/em><\/p>[\/et_pb_text][\/et_pb_column][et_pb_column type=”1_4″ _builder_version=”4.3.4″ custom_padding=”|50px||50px|false|false” custom_padding__hover=”|||”][et_pb_text _builder_version=”4.9.10″ background_color=”#FFFFFF” custom_margin=”60px|-33px|||false|false” custom_padding=”50px|10px|10px|10px|false|false” border_radii=”on|12px|12px|12px|12px”]

CONTACTEZ-NOUS<\/h2>[\/et_pb_text][et_pb_text _builder_version=”4.9.10″ background_color=”rgba(239,107,0,0.98)” custom_margin=”-30px|-28px|||false|false” custom_padding=”20px|15px|20px|15px|false|false” link_option_url=”mailto:info-cru.neuro@mcgill.ca” border_radii=”on|12px|12px|12px|12px”]

Contactez info-cru.neuro@mcgill.ca<\/span><\/a><\/strong><\/span><\/h3>[\/et_pb_text][et_pb_text _builder_version=”4.9.10″ background_color=”#FFFFFF” width=”100%” custom_margin=”60px||||false|false” custom_padding=”10px|10px|10px|10px|false|false” border_radii=”on|12px|12px|12px|12px”]

PLUS DE NOUVELLES…<\/h2>[\/et_pb_text][et_pb_blog posts_number=”3″ include_categories=”45″ use_manual_excerpt=”off” excerpt_length=”0″ show_more=”on” show_author=”off” show_date=”off” show_categories=”off” show_excerpt=”off” _builder_version=”4.9.10″ _module_preset=”default” header_level=”h4″ body_line_height=”1em” meta_line_height=”1em” read_more_text_color=”#4B0084″ read_more_line_height=”1em” pagination_text_color=”#4B0084″ pagination_line_height=”1em” min_height=”1000px” height=”100px” max_height=”100px” custom_margin=”-20px||-60px||false|false” custom_padding=”0px||50px||false|false” border_radii_image=”on|12px|12px|12px|12px”][\/et_pb_blog][\/et_pb_column][\/et_pb_row][\/et_pb_section][et_pb_section fb_built=”1″ _builder_version=”4.9.10″ _module_preset=”default”][\/et_pb_section]\n","protected":false},"excerpt":{"rendered":"

About Us Meet the team Principal Investigators Trials Recruiting ALS Autism Brain Tumour Dementia Epilepsy Intensive Care Unit Migraine Movement Disorders Multiple Sclerosis Neuromuscular Neuro-Surgery Stroke Patients Professionals News Careers Contact us FR 2024: Le Neuro \u00e9largit son offre d’essais cliniques testant des th\u00e9rapies cibl\u00e9es pour les maladies g\u00e9n\u00e9tiques \u00a0 Sophie Lorenzo19 d\u00e9cembre 2024 Cette […]<\/p>\n","protected":false},"author":12,"featured_media":8610,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_et_pb_use_builder":"on","_et_pb_old_content":"","_et_gb_content_width":"2880","_monsterinsights_skip_tracking":false,"_monsterinsights_sitenote_active":false,"_monsterinsights_sitenote_note":"","_monsterinsights_sitenote_category":0},"categories":[51,257,253,16,251],"tags":[],"yoast_head":"\nRetour sur les avanc\u00e9es de 2024 - Clinical Research Unit<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/cru.mcgill.ca\/fr\/retour-sur-2024\/\" \/>\n<meta property=\"og:locale\" content=\"en_US\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Retour sur les avanc\u00e9es de 2024 - 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