RNA therapy could offer a new approach to treat Charcot-Marie-Tooth

About Us CRU Directors CRU Investigators Leading Trial Site Trials Recruiting ALS Brain Tumour Dementia Epilepsy Intensive Care Unit Movement Disorders Multiple Sclerosis Neuromuscular Stroke Patients Advanced Therapies ASHG SYMPOSIUM Registration Program Abstracts...

A look back at the advances of 2024

About Us CRU Directors CRU Investigators Leading Trial Site Trials Recruiting ALS Autism Brain Tumour Dementia Epilepsy Intensive Care Unit Migraine Movement Disorders Multiple Sclerosis Neuromuscular Neuro-Surgery Stroke Patients Advanced Therapies ASHG SYMPOSIUM...

Big changes ahead for myotonic dystrophy treatments

About Us CRU Directors CRU Investigators Leading Trial Site Trials Recruiting ALS Brain Tumour Dementia Epilepsy Intensive Care Unit Movement Disorders Multiple Sclerosis Neuromuscular Stroke Patients Advanced Therapies ASHG SYMPOSIUM Registration Program Abstracts...

Finding the master switch to turn off ALS

About Us CRU Directors CRU Investigators Leading Trial Site Trials Recruiting ALS Brain Tumour Dementia Epilepsy Intensive Care Unit Movement Disorders Multiple Sclerosis Neuromuscular Stroke Patients Advanced Therapies ASHG SYMPOSIUM Registration Program Abstracts...