PRELIMINARY PROGRAM

9:00-9:15  | WELCOME AND OPENING REMARKS

9:15-10:30 | KEYNOTE

1. 1. First-in-human Trial with CRISPR Gene Editing Therapy
   2. 40 Years of Innovation in Clinical Research at The Neuro

10:30-11:00 | Coffee Break

11:00-12:15 | GENE AND GENE-EDITING THERAPIES

1. 1. Base Editing in Rare Neurological Disorders
   2. Prime Editing as a Versatile Tool for Gene Therapy
   3.  Gene Therapy for Leukodystrophies

12:15-1:45 | Lunch + Poster Session

1:45-3:00| PROMISE + CHALLENGES OF CELL THERAPY

1. 1. CAR-T for Brain Tumours
   2.  Cell Therapy for Parkinson’s Disease
   3. Cell Therapy for Neuroinflammatory Disease

3:00-3:15 | Coffee Break

3:15-4:30  | NOTES FROM A DECADE OF RNA THERAPEUTICS

1. 1. The Success of RNA in Treating Spinal Muscular Atrophy
   2. Advanced Delivery Methods for RNA Therapies
   3. ASOs for Ultra-rare Neurodevelopmental Disorders

4:30-6:00  | Networking Cocktail