PRELIMINARY PROGRAM

9:00-9:15  | WELCOME + OPENING REMARKS

9:15-10:30 | KEYNOTE

1. 1. First-in-human Trial with CRISPR Gene Editing Therapy
          Fyodor Urnov, University of California, Berkeley
   2. 40 Years of Innovation in Clinical Research at The Neuro
      Massimo Pandolfo, Medical Director, CRU, The Neuro

10:30-11:00 | Coffee Break

11:00-12:15 | GENE + GENE-EDITING THERAPIES

1. 1. Base Editing in Rare Neurological Disorders
      Jagdeep Walia, Queens University
   2. Prime Editing as a Versatile Tool for Gene Therapy
   3.  Gene Therapy for Leukodystrophies

12:15-1:45 | Lunch + Poster Session

1:45-3:00| PROMISE + CHALLENGES OF CELL THERAPY

1. 1.  Cell Therapy for Parkinson’s Disease
      Andres Lozano, University of Toronto
   2. CAR-T for Brain Tumours
      
   3. Cell Therapy for Neuroimmunological Diseases

3:00-3:15 | Coffee Break

3:15-4:30  | NOTES FROM A DECADE OF RNA THERAPEUTICS

1. 1. The Success of RNA in Treating Spinal Muscular Atrophy
      Maryam Oskoui, McGill University Health Centre
   2. Advanced Delivery Methods for RNA Therapies
   3. ASOs for Ultra-rare Neurodevelopmental Disorders

4:30-6:00  | Networking Cocktail